【文件属性】：
文件名称：In this issue[hellip]
文件大小：41KB
文件格式：PDF
更新时间：2021-06-29 17:54:36
学术 论文
In this issue[hellip]
T h e J o u r n a l o f
G E N E M E D I C I N E
In this issue¼
Gene therapy for hemophilia
± a review
Hemophilia A and B are X-linked
recessive bleeding disorders that result
from a de:registered:ciency in factor VIII (FVIII)
and factor IX (FIX), respectively.
Though factor substitution therapy
has greatly improved the lives of
hemophilic patients, there are still
limitations to the current treatment
that have triggered interest in alter-
native approaches by gene ther